Therapeutic intervention for Niemann–Pick type C disease must target
Por um escritor misterioso
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Combination therapy a potential strategy for treating Niemann-Pick disease
Niemann-Pick disease A or B in four pediatric patients and SMPD1 mutation carrier frequency in the Mexican population
New murine Niemann-Pick type C models bearing a pseudoexon-generating mutation recapitulate the main neurobehavioural and molecular features of the disease
Targeting defective sphingosine kinase 1 in Niemann–Pick type C disease with an activator mitigates cholesterol accumulation - Journal of Biological Chemistry
Niemann-Pick disease type C – topic of research paper in Biological sciences. Download scholarly article PDF and read for free on CyberLeninka open science hub.
Immune dysfunction in Niemann‐Pick disease type C - Platt - 2016 - Journal of Neurochemistry - Wiley Online Library
Niemann-Pick Disease, A Pipeline Analysis Report 2018, Technavio
Niemann-Pick type C disease: molecular mechanisms and potential therapeutic approaches. - Abstract - Europe PMC
Cureus, Niemann-Pick Disease: A Case Report and Literature Review
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