Generation of HEXA-deficient hiPSCs from fibroblasts of a Tay
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Descrição
Human iPSC line TSD-01-hiPSC was generated from fibroblasts of a patient with infantile Tay-Sachs disease (TSD). The patient is compound heterozygous …
Generation and characterization of patient-specific induced pluripotent
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PDF) New Approaches to Tay-Sachs Disease Therapy
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PDF) New Approaches to Tay-Sachs Disease Therapy
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